Leuprolide (Lupron) - GnRH Agonist for Androgen Deprivation Therapy — Reproduction

FDA-approved GnRH agonist for advanced prostate cancer, endometriosis, uterine fibroids, and precocious puberty via testosterone/estrogen suppression.

Overview

Leuprolide acetate (Lupron) is a synthetic gonadotropin-releasing hormone (GnRH) agonist FDA-approved for advanced prostate cancer (androgen deprivation therapy), endometriosis, uterine fibroids, and central precocious puberty. Paradoxical mechanism: initial GnRH receptor stimulation causes brief testosterone/estrogen surge, followed by receptor downregulation and sustained suppression of LH/FSH secretion. Phase 3 trials show 99.4% achieve castrate testosterone levels (≤50 ng/dL) by day 28, with 94% maintaining ≤20 ng/dL throughout treatment. Available in 1-month, 3-month, 4-month, and 6-month depot formulations for convenience. In men, induces medical castration for prostate cancer. In women, suppresses estrogen for endometriosis/fibroids. Standard first-line hormonal therapy for advanced/metastatic prostate cancer.

Indications

  • Advanced prostate cancer (palliative androgen deprivation therapy)
  • Endometriosis (pre-surgical or symptom management)
  • Uterine leiomyomata (fibroids) - pre-operative shrinkage
  • Central precocious puberty (children)
  • Gender-affirming hormone therapy (off-label, feminizing regimens)

Mechanism of Action

Prostate cancer: testosterone-dependent growth. Endometriosis/fibroids: estrogen-dependent

Dosing

CompoundDoseFrequencyNotes
Leuprolide acetate 7.5 mg depot7.5 mg IMEvery 4 weeks (monthly)Add bicalutamide 50 mg PO daily for first 4 weeks to prevent testosterone flare
Leuprolide acetate 22.5 mg depot22.5 mg SC or IMEvery 12 weeks (quarterly)Equivalent efficacy to monthly; reduces injection frequency; add antiandrogen for first dose
Leuprolide acetate 45 mg depot45 mg SCEvery 24 weeks (semi-annually)Only 2 injections/year; 93.4% achieve testosterone ≤50 ng/dL from week 4-48
Leuprolide acetate 3.75 mg depot3.75 mg IMEvery 4 weeksMaximum 6 months duration; add-back therapy (estrogen/progesterone) to reduce bone loss and hot flashes
Leuprolide acetate 11.25 mg depot11.25 mg IMEvery 12 weeksPre-operative shrinkage; maximum 3-6 months

Evidence Grade

GRADE A

Safety & Contraindications

  • ⚠️ PRESCRIPTION MEDICATION - Oncology/endocrinology supervision required
  • TESTOSTERONE FLARE in first 2-3 weeks: Initial LH surge causes transient ↑testosterone (may worsen bone pain, urinary obstruction, spinal cord compression in prostate cancer) - add antiandrogen (bicalutamide) for first 4 weeks
  • Cardiovascular risks: Increased risk of myocardial infarction, stroke, sudden cardiac death with long-term ADT - monitor cardiovascular risk factors
  • Metabolic syndrome: Weight gain, insulin resistance, dyslipidemia, diabetes risk
  • Bone loss: Significant osteoporosis risk with long-term use - DEXA screening, calcium/vitamin D, consider bisphosphonates
  • Hot flashes (80%): Most common side effect; may use low-dose estrogen patch or venlafaxine
  • Sexual dysfunction: Erectile dysfunction, loss of libido (expected effect)
  • Depression, cognitive changes, fatigue: Common with long-term ADT
  • In women: Menopausal symptoms, bone loss, mood changes
  • NOT for pregnancy (Category X); use contraception during treatment